Gene transfer into stem cell

Giuliana Ferrari

Giuliana Ferrari

Location: DIBIT1 A2, Floor 2, Room 31

Group leader, Gene transfer into stem cell Unit
Full professor, Università Vita-Salute San Raffaele
Scientific Director, GLP Test Facility

Giuliana Ferrari is Professor of Molecular Biology and Gene Expression Regulation at the San Raffaele University School of Medicine, Group leader and Director of GLP facility at the San Raffaele Telethon Institute for Gene Therapy (Milan, Italy).

Her fields of interest and research are engineering of viral vectors, transcriptional regulation, development of preclinical models for gene therapy, gene therapy for beta-thalassemia and  hematopoietic stem cell biology. She is an internationally recognized expert on gene therapy for hematopoietic diseases and thalassemia and leads the gene therapy clinical trial TIGET BTHAL (NCT02453477).

She has been working in the field of gene transfer and gene therapy for genetic diseases from the beginning of her career. Recently, she accomplished the clinical translation of gene therapy for beta-thalassemia, starting from the development of transcriptionally regulated beta-globin lentiviral vectors to patients’ treatment. Along with her research in the field of translational science, she pursues fundamental stem cell research, focused on understanding regulation of hematopoietic hierarchy and erythropoiesis in genetic anemia, and the composition of bone marrow niche and its interaction with hematopoietic stem cells.

She is regularly invited as speaker at national and international scientific meetings. For her scientific achievements in the field of thalassemia, in 2018 Giuliana Ferrari received the prestigious Rosa Camuna Award from Regione Lombardia, that is assigned each year to individuals that made a particular impact in the economic, social, cultural and sport development of the region. In 2021, she has been nominated European Chair of ATMP platform at EATRIS (