EC approval for Libmeldy
Developed thanks to more than 15 years of research by the San Raffaele Telethon Institute for Gene Therapy in Milan, Libmeldy is the first therapy approved for eligible patients with early-onset MLD
MOREEffective antibodies against SARS-CoV-2
Discovered a group of antibodies associated with reduced mortality in Covid-19 patients
MORE3D models to study Chronic Lymphocytic Leukemia
Researchers seek to understand how cancer cells interact with the microenvironment
MOREHighlights
Gene editing: getting closer to clinical application for a rare genetic disease
New study demonstrates that CRIPSR-Cas9 is able to correct the genetic defect underlying...
A prestigious ERC grant awarded to Raffaella Di Micco
Di Micco’s project will investigate how blood stem cells respond to genetic...
Covid-19: discovered hidden immune weakness in gravely ill patients
An international research consortium reveals genetic and immunological predispositions in...
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